Gene therapy helps boys with ‘Lorenzo’s Oil’ disease

In this Aug. 29, 2017 photo provided by Boston Children’s Hospital, Brian Rojas smiles while standing next to his brother Brandon at Boston Children’s Hospital. The boys suffer from adrenoleukodystrophy, an inherited nerve disease featured in the movie “Lorenzo’s Oil.” Brian was able to benefit from an experimental treatment while the disease had progressed too far in Brandon to qualify for the gene therapy study. Study results were published Wednesday, Oct. 4 by the New England Journal of Medicine and discussed at the Child Neurology Society conference in Kansas City. (Katherine C. Cohen/Boston Children’s Hospital via AP)